Programme

Selected talks:

Nadav Ahituv, University of California, San Francisco, USA – “Functional characterization and therapeutic targeting of gene regulatory elements”

Pascale Bouillé, Flash Therapeutics, France – “The same lentiviral platform for efficient DNA or RNA delivery”

Reetta Hinttala, University of Oulu, Finland – “Geno-phenotype discoveries of rare diseases among the Finns”

Ophir Klein, University of California, San Francisco, USA – “tba”

Stanislav Kmoch, First Faculty of Medicine, Charles University, Czech Republic – “Finding the genetic causes of chronic kidney disease”

Len Pennacchio, Lawrence Berkeley National Laboratory, United States – “In Vivo Studies of Human Genome Function”

Damian Smedley, Queen Mary University of London, United Kingdom – “Phenotype-based diagnostics and discovery in rare disease”

Tomas Stopka, First Faculty of Medicine, Charles University, Czech Republic – “tba”

Seppo Ylä-Herttuala, University of Eastern Finland, Finland – “Models and preclinical gene therapy program in familial hypercholesterolemia”